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ELAD

Liraglutide in mild to moderate Alzheimer's disease: a phase 2b clinical trial (Evaluating Liraglutide in Alzheimer's Disease — ELAD)

Year of Publication: 2026

Authors: Edison P, Femminella GD, Ritchie CW, ..., Harrison J

Journal: Nature Medicine

Citation: Nat Med. 2026 Jan;32(1):353–363. doi:10.1038/s41591-025-04106-7. ClinicalTrials.gov NCT01843075.

Link: https://doi.org/10.1038/s41591-025-04106-7

Bottom Line

Liraglutide 1.8 mg SC daily for 52 weeks did NOT reduce decline in cerebral glucose metabolism (primary outcome) in mild-to-moderate Alzheimer's disease, but showed an exploratory cognitive benefit on the composite ADAS-Exec (Δ 0.15 z-score; 95% CI 0.03–0.28; unadjusted P=0.01) and less temporal-lobe and gray-matter atrophy. Safety was acceptable, with fewer serious AEs than placebo (6.9% vs 17.6%) and the expected GI/weight-loss profile.

Major Points

  • Largest randomized Phase 2b trial of a GLP-1 receptor agonist in Alzheimer's disease to date (n=204, 24 UK sites, 12-month treatment) — the ELAD trial.
  • Negative for the imaging primary outcome: composite cerebral glucose metabolic rate (FDG-PET SUV across hippocampus, medial temporal lobe, posterior cingulate) — adjusted Δ −0.17 (95% CI −0.39 to 0.06), P=0.14; spectral-analysis sensitivity confirmed.
  • Positive cognitive secondary signal on ADAS-Exec (composite of ADAS-Cog + NTB Executive z-scores): liraglutide arm declined 0.15 SD less than placebo (95% CI 0.03–0.28), unadjusted P=0.01. CDR-SoB and ADCS-ADL not different.
  • Exploratory MRI: liraglutide associated with attenuated temporal lobe atrophy (Δ 696 mm³, 95% CI 184–1208, P<0.001), less whole gray matter loss (Δ 7,274 mm³, P=0.002), and trends in parietal and frontoparietal lobes. No hippocampal or entorhinal differences.
  • Safety: total AEs slightly higher with liraglutide (541 vs 450) driven by GI events (25.5% of all liraglutide AEs); serious AEs were LESS frequent on liraglutide — 6.9% (7/102) vs 17.6% (18/102) placebo. Weight loss ≥5%: 48.1% liraglutide vs 13.7% placebo.
  • Findings are exploratory and not multiplicity-corrected; reduced sample size (vs original power calculation) and 30% drop-off of analyzable scans in the treatment arm limit definitive conclusions. Larger confirmatory Phase 3 trials of GLP-1 analogs in AD are warranted (oral formulation may improve tolerability).

Design

Study Type: Multicenter, double-blind, placebo-controlled, randomized Phase 2b clinical trial

Randomization: 1

Blinding: Double-blind (participants, investigators, outcome assessors)

Enrollment Period: March 2014 to January 2021

Follow-up Duration: 52 weeks (with optional 12-month open-label extension, not reported here)

Centers: 24

Countries: United Kingdom

Sample Size: 204

Analysis: Intention-to-treat; ANCOVA for primary outcome adjusting for baseline value and stratification factors (age, MMSE); multilevel mixed-effects model for cognitive secondary outcomes; no imputation of missing outcome data


Inclusion Criteria

  • Age 50 years or older
  • Clinical diagnosis of probable Alzheimer's disease per NINCDS-ADRDA criteria, supported by clinical history, neurological exam, neuropsychometric testing, and MRI
  • Mini-Mental State Examination (MMSE) score ≥15 (i.e., mild-to-moderate dementia)
  • Clinical Dementia Rating (CDR) Global score of 0.5, 1, or 2 (calculated via University of Washington online algorithm)
  • Capacity to provide written informed consent (or appropriate proxy where required)

Exclusion Criteria

  • Diabetes mellitus requiring pharmacologic treatment (any antidiabetic agent)
  • Inability to tolerate FDG-PET or MRI scanning
  • Significant non-Alzheimer neurological or psychiatric illness contributing to cognitive impairment
  • Conditions or medications interfering with study procedures or GLP-1 analog safety (e.g., personal/family history of medullary thyroid cancer, MEN2, history of pancreatitis — per Victoza label)
  • Pregnancy or lactation
  • Participation in another interventional trial

Baseline Characteristics

CharacteristicPlacebo (n=102)Liraglutide (n=102)
Female sex39 (38%)42 (41%)
Mean Age (years)72.5 ± 7.070.6 ± 8.4
Education (years)12.9 ± 3.013.1 ± 4.2
MMSE23.4 ± 3.623.7 ± 3.5
ADAS-Cog 1331.9 ± 9.331.6 ± 10.3
CDR-SoB3.6 ± 1.83.7 ± 1.9
ADCS-ADL66.1 ± 9.766.5 ± 9.5
NPI (total)7.5 ± 9.010.2 ± 12.5
GDS5.5 ± 4.45.4 ± 4.0
COWAT11.5 ± 4.99.8 ± 4.2
Category Fluency10.5 ± 4.810.3 ± 5.5
TMT-A71.2 ± 52.378.2 ± 58.0
TMT-B148.8 ± 78.4149.0 ± 80.6
Digit Span Forward8.8 ± 2.28.0 ± 2.4
Digit Span Backward5.3 ± 2.35.0 ± 2.2
Insulin (median, IQR)6.2 (4.1–8.7)6.9 (4.4–9.1)
Lipase U/L (median, IQR)40.5 (34.0–53.0)46.0 (33.0–68.5)
Amylase U/L80.1 ± 50.380.7 ± 58.3

Arms

FieldLiraglutideControl
n102102
InterventionSubcutaneous liraglutide, escalated from 0.6 mg/day to 1.8 mg/day over 4 weeks (if 1.8 mg not tolerated, 1.2 mg/day for 2 more weeks before re-attempting 1.8 mg)Matching placebo subcutaneous injection on identical titration schedule
Duration52 weeks (optional 12-month open-label extension)52 weeks

Outcomes

OutcomeTypeControlInterventionHR / OR / RRP-value
Change in cerebral glucose metabolic rate (rCMRglc) on [18F]FDG-PET in a composite cortical ROI (hippocampus + medial temporal lobe + posterior cingulate) from baseline to 52 weeks (SUV method, ANCOVA adjusted for baseline, age, MMSE)PrimaryReference (placebo)Δ vs placebo: −0.170.14
ADAS-Exec composite z-score (ADAS-Cog + Executive NTB domain) at 52 wkSecondary0.01 (unadjusted)
CDR-Sum of Boxes change at 52 wkSecondary0.81
ADCS-ADL change at 52 wkSecondary0.65
Treatment-emergent AEs / SAEs (key secondary)SecondaryLiraglutide: 541 AEs in 88 pts; SAEs 7 (6.9%) in 7 pts · Placebo: 450 AEs in 87 pts; SAEs 25 in 18 (17.6%) pts · Note: Fewer SAEs with liraglutide
Total AEsAdverseLiraglutide 541 (in 88/102 = 86%) vs Placebo 450 (in 87/102 = 85%)
Serious AEs (participants with ≥1)AdverseLiraglutide 7/102 (6.9%) vs Placebo 18/102 (17.6%)
Unexpected SAEsAdverseLiraglutide 4 vs Placebo 14
Life-threatening SAEAdverse0 vs 1 (placebo)
GI disorders (proportion of all AEs in arm)AdverseLiraglutide 25.5% (most common AE category)
Common GI side effectsAdverseAnorexia, bloating, diarrhea, dyspepsia, nausea
Weight loss ≥5% to <10%AdverseLiraglutide 39.2% vs Placebo 12.6%
Weight loss 5–10%AdverseLiraglutide 8.9% vs Placebo 1.1%

Subgroup Analysis

Analyzable patients with MMSE ≤18 (n=23) vs >18 (n=181) reported in Supplementary Tables 1–2; treatment effect described as exploratory and consistent. No prespecified subgroup met efficacy threshold for FDG-PET primary endpoint.


Criticisms

  • Primary outcome (FDG-PET SUV change) was NEGATIVE; the positive cognitive signal on ADAS-Exec was an unadjusted, exploratory secondary endpoint and should be interpreted as hypothesis-generating.
  • Achieved sample size and analyzable-scan numbers fell below the original power calculation (only 72 of 102 treatment-arm participants had analyzable week-52 scans), reducing statistical power for the primary endpoint.
  • Differential attrition: 70.6% of liraglutide vs 80.4% of placebo had analyzable scans at week 52 — potential informative dropout.
  • Population was overwhelmingly White (only 4/204 identified as non-White), limiting generalizability across ethnic groups; UK-only, single tertiary imaging center.
  • Study drug discontinued 3 days before week-52 PET (rationale: minimize acute glucose effects), which may have masked any short-term metabolic benefit and differs from a prior 26-week pilot that maintained dosing through scan.
  • ELAD did NOT enroll diabetics — efficacy in the AD + T2D population (where signal in prior post-hoc analyses was strongest) was not tested.
  • Once-daily subcutaneous injections impose substantial trial burden — future Phase 3 trials of oral semaglutide (e.g., EVOKE/EVOKE+) will be more clinically translatable.
  • Enrollment spanned 2014–2021 (including COVID-19 disruption), and follow-up MRI/PET volumes are exploratory — confirmatory data needed.

Funding

Investigator-initiated trial led by Imperial College London; supported by Alzheimer's Society UK and UK Medical Research Council with additional academic support. Liraglutide and matching placebo provided by Novo Nordisk. PI P. Edison reports funding from MRC/HEFCE and unrestricted academic grants. Full disclosures in publication.

Based on: ELAD (Nature Medicine, 2026)

Authors: Edison P, Femminella GD, Ritchie CW, ..., Harrison J

Citation: Nat Med. 2026 Jan;32(1):353–363. doi:10.1038/s41591-025-04106-7. ClinicalTrials.gov NCT01843075.

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